Total submissions: 3
| Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
|---|---|---|---|---|---|---|---|---|
| Laboratory of Diagnosis and Therapy of Lysosomal Disorders, |
RCV000011240 | SCV005089027 | pathogenic | Mucopolysaccharidosis, MPS-II | 2024-06-07 | criteria provided, single submitter | literature only | Prevalence of the variant significantly increased in affected individuals compared with controls (PS4_Supporting), Located in a mutational hot spot and/or critical functional domain (PM1_Moderate), Absent from controls (or at low frequency) in gnomAD database (PM2_Moderate), Missense variant in a gene with a low rate of benign missense variation (PP2_Supporting), Multiple lines of computational evidence support a deleterious effect (PP3_Supporting), Patient’s phenotype or family history highly specific for the disease (PP4_Strong) |
| Baylor Genetics | RCV000011240 | SCV003835259 | likely pathogenic | Mucopolysaccharidosis, MPS-II | 2022-08-19 | criteria provided, single submitter | clinical testing | |
| OMIM | RCV000011240 | SCV000031467 | pathogenic | Mucopolysaccharidosis, MPS-II | 1992-08-01 | no assertion criteria provided | literature only |